This program is working to advance a gene delivery vehicle that targets cells in the lung. 4D-710 is a customized adeno-associated virus (AAV) vector designed to deliver a healthy CFTR gene specifically to cells in the lungs of people with CF. This would allow the lung cells to create normally functioning CFTR protein, regardless of an individual’s specific CFTR gene mutation.
Laboratory studies to develop and test this potential therapy are underway.
This program is sponsored by 4D Molecular Therapeutics and partially funded by the Cystic Fibrosis Foundation.
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