Lives unaffected by cystic fibrosis

DRUG DEVELOPMENT PIPELINE

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4D Molecular Therapeutics

Pre-clinical

Pre-clinical

Therapeutic Approach

Restore CFTR Function

This program is working to advance a gene delivery vehicle that targets cells in the lung. 4D-710 is a customized adeno-associated virus (AAV) vector designed to deliver a healthy CFTR gene specifically to cells in the lungs of people with CF. This would allow the lung cells to create normally functioning CFTR protein, regardless of an individual’s specific CFTR gene mutation.

Status

Laboratory studies to develop and test this potential therapy are underway.

Sponsor

This program is sponsored by 4D Molecular Therapeutics and partially funded by the Cystic Fibrosis Foundation.



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